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A 60-year-old with heart failure has preserved ejection fraction but severe diastolic dysfunction. Biopsy reveals amyloid deposits. Genetic testing confirms hereditary transthyretin amyloidosis.

Heterogeneous

  • TNNI3, MYH7 (sarcomeric)
  • DES (desmin)
  • TTR (transthyretin amyloidosis)
  • Diastolic dysfunction with preserved (or mildly reduced) EF
  • Stiff ventricles, restrictive filling
  • Biatrial enlargement
  • Poor prognosis
  • Echo shows preserved (or near-normal) ejection fraction and non-dilated ventricles with marked diastolic dysfunction and biatrial enlargement
  • The key distinction is from constrictive pericarditis, resolved with cardiac MRI and invasive hemodynamics
  • Workup targets the underlying cause: Tc-99m PYP scintigraphy for transthyretin amyloid, endomyocardial biopsy when infiltrative disease is suspected, and gene testing (TNNI3, MYH7, DES, TTR)
  • Treat the underlying cause when one is identified (for example, TTR stabilizers or silencers in transthyretin amyloidosis)
  • Cautious diuresis for congestion, rate control, and management of atrial fibrillation including anticoagulation
  • Prognosis is generally poor; evaluate selected patients for heart transplant

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