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A newborn or young infant with reduced postural tone. Classic findings: head lag on traction, "frog-leg" posture at rest, slipping through the examiner's hands on vertical suspension, a U-shape on ventral suspension. "Floppy" is a chief-complaint word; the work is in localizing where the floppiness comes from.

This is the single most useful bedside distinction and shapes the entire work-up.

FeatureCentral (brain)Peripheral (motor unit)
Mental statusOften depressed, less interactiveAlert, engaged, frustrated
ReflexesPreserved or briskReduced or absent
Antigravity strengthWeakness less prominent than toneProfound; can't lift limb against gravity
FasciculationsAbsentMay be present (especially tongue in SMA)
Cry / suckUsually normalWeak
Respiratory effortUsually adequateDiaphragmatic, paradoxical, fatigues
Dysmorphic featuresCommon (syndromic)Usually absent

Rule of thumb: central hypotonia outnumbers peripheral roughly 2:1. But peripheral causes are more often urgent and more often have disease-modifying therapy now, so don't anchor.

The brain is "running the body softly." Look for dysmorphism, anomalies, encephalopathy, seizures.

  • Down syndrome: most common chromosomal cause of neonatal hypotonia; usually obvious on exam.
  • Prader-Willi syndrome: severe neonatal hypotonia plus poor feeding that later evolves into hyperphagia; almond eyes, narrow bifrontal diameter. Methylation testing is the single best first-line test.
  • Hypoxic-ischemic encephalopathy: perinatal event, low Apgars, multisystem injury.
  • Congenital infections (TORCH): microcephaly, intracranial calcifications, organomegaly.
  • Zellweger spectrum: high forehead, large fontanelle, hepatomegaly plus seizures plus profound hypotonia. VLCFAs are the first-line test.
  • Mitochondrial disease (Leigh, others): lactic acidosis, multisystem.

The brain is fine; the lesion is below it. Anatomy from proximal to distal:

Anterior horn cell

  • Spinal muscular atrophy (SMA): the must-not-miss diagnosis. Symmetric proximal weakness, tongue fasciculations, areflexia, preserved facial movement. Newborn screening covers it in most US states. Disease-modifying therapies (nusinersen, onasemnogene abeparvovec, risdiplam) work best when started early. Send SMN1 deletion testing today.

Peripheral nerve

Neuromuscular junction

  • Congenital myasthenic syndromes: fluctuating weakness, fatigability, ptosis. Distinguish from transient neonatal myasthenia (mother has MG; resolves).

Muscle

  • Pompe disease (GSD type II): hypertrophic cardiomyopathy plus profound weakness. Acid α-glucosidase activity is the diagnostic test; treatable with ERT, so don't miss it.
  • Myotonic dystrophy type 1, congenital form: almost always inherited from the mother (anticipation). Tented upper lip, polyhydramnios history, severe weakness, talipes. Check mom for grip myotonia.
  • Congenital muscular dystrophies (α-dystroglycanopathies, LAMA2): early weakness with elevated CK; some have brain and eye involvement.
  • Mitochondrial myopathies: lactic acidosis with weakness.
  • Nemaline / congenital myopathies: biopsy-defined.
  • Respiratory distress, weak cry, paradoxical breathing → SMA or congenital muscular dystrophy until proven otherwise. Don't wait for the genetics; admit and monitor.
  • Hypertrophic cardiomyopathy + hypotonia → Pompe disease. ERT is most effective if started before 6 months.
  • Tongue fasciculations → SMA.
  • Massive hepatomegaly + neonatal seizures + dysmorphism → peroxisomal (Zellweger) or LSD.
  • Maternal grip myotonia → congenital myotonic dystrophy in the infant.

The right first test depends on the localization step above. A reasonable opening battery for an undifferentiated floppy infant:

  1. CK: elevated in muscle disease (Pompe, congenital MD), normal in anterior horn cell and central causes.
  2. SMA deletion testing (or trust the newborn screen if already done). Turnaround is fast, and a positive result changes management immediately.
  3. Karyotype + chromosomal microarray: Down syndrome, microdeletion syndromes.
  4. Methylation analysis at 15q11-q13 if Prader-Willi is on the table.
  5. VLCFAs if a peroxisomal disorder is suspected.
  6. Lactate, ammonia, acylcarnitines, urine organic acids for metabolic causes.
  7. MRI brain for central etiologies, especially with seizures or focal findings.

Exome / genome sequencing has overtaken the older tiered approach in most centers when the first-pass tests are unrevealing. Discuss timing with neurology and genetics.

  • Always examine the mother. Congenital myotonic dystrophy is the classic "you have to examine mom" diagnosis. Her grip myotonia clinches it before any genetic test runs.
  • Central hypotonia + normal CK is the most common combination by far, but the rare peripheral cases are the ones that earn you grudging respect later.
  • "Frog-leg posture with full alertness" is the SMA setup question on every exam.