StudyRareStudyRare

Alkaptonuria

Log in to star

Last updated 2mo ago

Log in to add personal notes on this page.

A 40-year-old presents with premature arthritis of the spine and large joints. His urine turns dark when left standing. On exam, his ear cartilage appears bluish-black (ochronosis).

AR; HGD (homogentisate 1,2-dioxygenase)

  • Dark urine (homogentisic acid oxidizes)
  • Ochronosis (bluish-black pigmentation of cartilage, sclera)
  • Premature degenerative arthritis (spine, large joints)
  • Cardiac valve disease
  • Kidney stones
  • Urine homogentisic acid elevated; dark urine on standing
  • Nitisinone (reduces homogentisic acid); symptomatic management

"Ow, my Knee Kap hurts a ton": "Ow-Kap-ton-uria" recalls the early-onset osteoarthritis from homogentisic acid toxicity to cartilage.

AKU = Arthritis, Kardiac Kalcification (aortic/mitral valve), Kidney stones, dArK Urine and Cartilage damage.

"Kartilage in alKaptonuria": homogentisic acid accumulates in cartilage. "Blkaptonuria": affected tissues (nose, ears, sclera, joints) are dark (ochronosis).

Reference Links