StudyRareStudyRare
Log in to add personal notes on this page.

A 4-year-old is diagnosed with adrenocortical carcinoma. Her mother had breast cancer at 32 and her maternal grandmother died of a brain tumor at 40. A TP53 pathogenic variant is identified.

AD; TP53 (tumor suppressor, "guardian of the genome")

  • ~70% inherited, ~30% de novo

Core Cancers (SBLA):

  • Sarcoma (bone and soft tissue)
  • Breast cancer (premenopausal)
  • Leukemia/lymphoma
  • Adrenal cortical carcinoma (childhood, highly associated)
  • Brain tumors (especially choroid plexus carcinoma)
  • Multiple primary cancers
  • Very early onset
  • Radiation sensitivity → avoid radiation when possible
  • Lifetime cancer risk >90%
  • Classic clinical criteria: a sarcoma before age 45, plus a first-degree relative with any cancer before age 45, plus a first- or second-degree relative with cancer before age 45 or a sarcoma at any age
  • The broader Chompret criteria prompt TP53 testing for early-onset core cancers (sarcoma, breast, brain, adrenocortical), multiple primaries, childhood adrenocortical carcinoma, or choroid plexus carcinoma regardless of family history
  • Confirm with germline TP53 testing; consider that an apparent germline variant can reflect clonal hematopoiesis or low-level mosaicism, which may need confirmation in a non-blood tissue
  • Intensive surveillance (whole-body MRI, brain MRI, biochemical markers)
  • Consider risk-reducing mastectomy
  • Avoid radiation when possible

SBLA cancers in Li-Fraumeni: Sarcoma, Breast, Leukemia/lymphoma, Adrenal cortical carcinoma. "TP53 = The Protector, 53 kDa"

TP53 visual: "5" looks like an "S" (sarcoma), "3" looks like a sideways B (brain tumors, breast). TP = Tumor Protein, the guardian of the genome.