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WAGR Syndrome (11p13 deletion)

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A newborn is noted to have aniridia. Given this finding, the provider orders a CMA which shows an 11p13 deletion. The care team initiates Wilms tumor surveillance.

  • Contiguous gene deletion: 11p13
  • Includes WT1 (Wilms tumor) and PAX6 (aniridia)

WAGR

  • Wilms tumor risk (~50%; highest risk under age 8)
  • Aniridia (absence of iris)
  • Genitourinary anomalies (cryptorchidism, hypospadias)
  • Range of developmental delays (as with most microdeletion syndromes)
  • Chromosomal microarray (CMA) is the first-line test and defines the extent of the 11p13 deletion, including involvement of WT1 and PAX6
  • Isolated aniridia warrants PAX6 and 11p13 evaluation; finding a contiguous WT1 deletion establishes WAGR and triggers Wilms tumor surveillance
  • WT1 involvement also raises the risk of nephropathy, so confirm whether WT1 is within the deleted segment
  • Wilms tumor surveillance: renal ultrasound every 3 months until age 8
  • Ophthalmologic evaluation

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