StudyRareStudyRare
Log in to add personal notes on this page.

A child with sparse, curly hair, hyperkeratotic skin, and congenital heart disease has distinctive coarse facial features and moderate to severe intellectual disability.

AD (de novo); BRAF (75%), MAP2K1, MAP2K2, KRAS

  • Overlap with Costello and Noonan
  • Hair: Sparse, curly, slow-growing
  • Skin: Hyperkeratosis, ichthyosis, keratosis pilaris
  • Cardiac: Pulmonary stenosis, HCM
  • Neuro: Moderate to severe ID (more severe than Noonan)
  • NO papillomata or tumor risk (unlike Costello)
  • Molecular confirmation of a (usually de novo) variant in BRAF, MAP2K1, MAP2K2, or KRAS, which also distinguishes CFC from Costello syndrome (HRAS) and Noonan syndrome (PTPN11)
  • Clinical recognition of the ectodermal findings (sparse curly hair, hyperkeratosis), congenital heart disease, and more severe intellectual disability
  • Cardiac surveillance for pulmonary valve stenosis and hypertrophic cardiomyopathy
  • Aggressive nutritional and gastrointestinal support; many infants have severe feeding difficulties requiring tube feeding
  • Seizure management plus developmental and educational support
  • Skin and ophthalmologic care
  • Unlike Costello syndrome, no tumor surveillance protocol is indicated

KardioFacioCutaneous (KFC) = KFC's BReakfast Menu: KRAS, BRAF, MAP2K1/MAP2K2.