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Hereditary multiple exostoses (HME)

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A 10-year-old boy has multiple bony lumps near the ends of his long bones, particularly around the knees. X-rays show multiple osteochondromas. His father has similar lesions.

AD; EXT1 (60-70%) or EXT2

  • Tumor suppressor genes (heparan sulfate biosynthesis)
  • Multiple osteochondromas (benign cartilage-capped bone tumors)
  • Near growth plates of long bones
  • May cause limb length discrepancy, angular deformity
  • Malignant transformation to chondrosarcoma: ~1-5% lifetime risk
  • Pain, nerve compression (some)
  • Radiographs: multiple osteochondromas arising from the metaphyses of long bones, with the lesion cortex and medulla continuous with the host bone
  • Clinical diagnosis when two or more osteochondromas plus a positive family history are present
  • EXT1 or EXT2 sequencing and deletion/duplication analysis confirms
  • New pain, growth of a lesion after skeletal maturity, or a thickened cartilage cap on imaging raises concern for chondrosarcoma; evaluate with MRI
  • Surgical excision of symptomatic osteochondromas causing pain, nerve or vessel compression, or functional impairment
  • Orthopedic management of limb-length discrepancy and angular deformity
  • Long-term surveillance for malignant transformation to chondrosarcoma; investigate any new growth or pain in adulthood

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